Recherche - Archive ouverte HAL Accéder directement au contenu

Filtrer vos résultats

19 résultats

Gene Therapy in Patients with the Crigler–Najjar Syndrome

Lorenzo D’antiga , Ulrich Beuers , Giuseppe Ronzitti , Nicola Brunetti-Pierri , Ulrich Baumann , et al.
New England Journal of Medicine, 2023, 389 (7), pp.620-631. ⟨10.1056/NEJMoa2214084⟩
Article dans une revue hal-04324294v1
Image document

Genetic-algorithm based framework for lattice support structure optimization in additive manufacturing

Benjamin Vaissier , Jean-Philippe Pernot , Laurent Chougrani , Philippe Veron
Computer-Aided Design, 2019, 110, pp.11-23
Article dans une revue hal-02294579v1

Prevalence and Relevance of Pre-Existing Anti-Adeno-Associated Virus Immunity in the Context of Gene Therapy for Crigler–Najjar Syndrome

Sem Aronson , Philippe Veron , Fanny Collaud , Aurélie Hubert , Virginie Delahais , et al.
Human Gene Therapy, 2019, 30 (10), pp.1297-1305. ⟨10.1089/hum.2019.143⟩
Article dans une revue hal-04324405v1
Image document

Systemic AAV8-Mediated Gene Therapy Drives Whole-Body Correction of Myotubular Myopathy in Dogs

David Mack , Karine Poulard , Melissa Goddard , Virginie Latournerie , Jessica Snyder , et al.
Molecular Therapy, 2017, 25 (4), pp.839-854. ⟨10.1016/j.ymthe.2017.02.004⟩
Article dans une revue hal-02179363v1
Image document

Early Phase Clinical Immunogenicity of Valoctocogene Roxaparvovec, an AAV5-Mediated Gene Therapy for Hemophilia A

Brian R Long , Philippe Veron , Klaudia Kuranda , Romain Hardet , Nina Mitchell , et al.
Molecular Therapy, 2021, 29 (2), pp.597-610. ⟨10.1016/j.ymthe.2020.12.008⟩
Article dans une revue hal-03200117v1

Prevalence and long-term monitoring of humoral immunity against adeno-associated virus in Duchenne Muscular Dystrophy patients

Christian Leborgne , Virginie Latournerie , Sylvie Boutin , Diana Desgue , Aliénor Quéré , et al.
Cellular Immunology, 2019, 342, pp.103780. ⟨10.1016/j.cellimm.2018.03.004⟩
Article dans une revue hal-04324449v1
Image document

Combining on-site and off-site analysis: towards a new paradigm for cultural heritage surveys

Violette Abergel , Kévin Jacquot , Livio De Luca , Philippe Veron
DISEGNARECON, 2021, 14 (26), ⟨10.20365/disegnarecon.26.2021.13⟩
Article dans une revue hal-03287495v1
Image document

Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy

Caroline C. Le Guiner , Laurent Servais , Marie Montus , Thibaut Thibaut , Bodvael Fraysse , et al.
Nature Communications, 2017, 8 (1), pp.16105. ⟨10.1038/ncomms16105⟩
Article dans une revue hal-02179396v1
Image document

Highly efficient transduction of human plasmacytoid dendritic cells without phenotypic and functional maturation.

Philippe Veron , Sylvie Boutin , Samia Martin , Laurence Chaperot , Joël Plumas , et al.
Journal of Translational Medicine, 2009, 7 (1), pp.10. ⟨10.1186/1479-5876-7-10⟩
Article dans une revue inserm-00367719v1
Image document

Prevalence and Relevance of Pre-Existing Anti-Adeno-Associated Virus Immunity in the Context of Gene Therapy for Crigler-Najjar Syndrome

S. J. Aronson , Philippe Veron , Fanny Collaud , Aurélie Hubert , Virginie Delahais , et al.
Human Gene Therapy, 2019, 30, pp.1297-1305. ⟨10.1089/hum.2019.143⟩
Article dans une revue hal-02880784v1
Image document

A generic formalism for the semantic modeling and representation of architectural elements

Livio De Luca , Philippe Veron , Michel Florenzano
The Visual Computer, 2007, 23 (3), pp.181-205. ⟨10.1007/s00371-006-0092-5⟩
Article dans une revue istex hal-01020092v1
Image document

Preclinical Development of an AAV8-hUGT1A1 Vector for the Treatment of Crigler-Najjar Syndrome

Fanny Collaud , Giulia Bortolussi , Laurence Guianvarc'H , Sem Aronson , Thierry Bordet , et al.
Molecular Therapy - Methods and Clinical Development, 2019, 12, pp.157-174. ⟨10.1016/j.omtm.2018.12.011⟩
Article dans une revue hal-02179298v1
Image document

Prevalence and long-term monitoring of humoral immunity against adeno-associated virus in Duchenne Muscular Dystrophy patients

Christian Leborgne , Virginie Latournerie , Sylvie Boutin , Diana Desgue , Aliénor Quéré , et al.
Cellular Immunology, 2018, pp.103780. ⟨10.1016/j.cellimm.2018.03.004⟩
Article dans une revue hal-02179236v1

Systemic AAV8-Mediated Gene Therapy Drives Whole-Body Correction of Myotubular Myopathy in Dogs

David Mack , Karine Poulard , Melissa Goddard , Virginie Latournerie , Jessica Snyder , et al.
Molecular Therapy, 2017, 25 (4), pp.839-854. ⟨10.1016/j.ymthe.2017.02.004⟩
Article dans une revue hal-04481609v1
Image document

Identification and validation of a 3D beam model of multi-stranded cables with a quasi-static robotic manipulation

Emmanuel Cottanceau , Olivier Thomas , Philippe Veron , Marc Alochet , Renaud Deligny
2020
Pré-publication, Document de travail hal-02973318v1
Image document

A Property Graph Data Model for a Context-Aware Design Assistant

Romain Pinquié , Philippe Veron , Frédéric Segonds , Thomas Zynda
16th IFIP International Conference on Product Lifecycle Management (PLM), Jul 2019, Moscow, Russia. pp.181-190, ⟨10.1007/978-3-030-42250-9_17⟩
Communication dans un congrès hal-03087028v1

503. Minimally Effective Dose of Systemic AAV8-MTM1 Needed To Prolong Survival and Correct Severe Muscle Pathology in a Canine Model of X-Linked Myotubular Myopathy

David Mack , Karine Poulard , Melissa Goddard , Jessica Snyder , Robert Grange , et al.
Molecular Therapy, 2015, 23, pp.S201. ⟨10.1016/S1525-0016(16)34112-0⟩
Article dans une revue hal-03159330v1

498. Prolonged Benefit from Systemic rAAV8 in a Canine Model of Myotubular Myopathy

Matthew Elverman , David Mack , Melissa Goddard , Jessica Snyder , Robert Grange , et al.
Molecular Therapy, 2016, 24, pp.S198. ⟨10.1016/S1525-0016(16)33307-X⟩
Article dans une revue hal-03158883v1
Image document

From the Semantic Point Cloud to Heritage-Building Information Modeling: A Semiautomatic Approach Exploiting Machine Learning

Valeria Croce , Gabriella Caroti , Livio De Luca , Kevin Jacquot , Andrea Piemonte , et al.
Remote Sensing, 2021, 13 (3), pp.461. ⟨10.3390/rs13030461⟩
Article dans une revue hal-03128295v1