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miR-379 links glucocorticoid treatment with mitochondrial response in Duchenne muscular dystrophy
Mathilde Sanson
,
Ai Vu Hong
,
Emmanuelle Massourides
,
Nathalie Bourg
,
Laurence Suel
,
et al.
Article dans une revue
inserm-02881214v1
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A Mouse Model for Monitoring Calpain Activity under Physiological and Pathological Conditions
Marc Bartoli
,
Nathalie Bourg
,
Daniel Stockholm
,
F. Raynaud
,
Antony Delevacque
,
et al.
Article dans une revue
hal-03674304v1
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Cis -splicing and Translation of the Pre- Trans -splicing Molecule Combine With Efficiency in Spliceosome-mediated RNA Trans -splicing
François Monjaret
,
Nathalie Bourg
,
Laurence Suel
,
Carinne Roudaut
,
Florence Le Roy
,
et al.
Article dans une revue
hal-02336897v1
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Identification of thiostrepton as a pharmacological approach to rescue misfolded alpha-sarcoglycan mutant proteins from degradation
Lucile Hoch
,
Sara F Henriques
,
Celine Bruge
,
Justine Marsolier
,
Manon Benabides
,
et al.
Article dans une revue
hal-02138777v1
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NF-kappa B-dependent expression of the antiapoptotic factor c-FLIP is regulated by calpain 3, the protein involved in limb-girdle muscular dystrophy type 2A
Beatrice Benayoun
,
Stephen Baghdiguian
,
Alicia Lajmanovich
,
Marc Bartoli
,
Nathalie Danièle
,
et al.
Article dans une revue
hal-01610041v1
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Efficient recovery of dysferlin deficiency by dual adeno-associated vector-mediated gene transfer
William Lostal
,
Marc Bartoli
,
Nathalie Bourg
,
Carinne Roudaut
,
Azéddine Bentaib
,
et al.
Article dans une revue
istex
hal-01610036v1
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Calcium-dependent plasma membrane repair requires m- or mu-calpain, but not calpain-3, the proteasome, or caspases
Ronald L. Mellgren
,
Katsuya Miyake
,
Irina Kramerova
,
Melissa J. Spencer
,
Nathalie Bourg
,
et al.
Article dans une revue
hal-01610039v1
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Cardiac ankyrin repeat protein is a marker of skeletal muscle pathological remodelling
Lydie Laure
,
Laurence Suel
,
Carinne Roudaut
,
Nathalie Bourg
,
Ahmed Ouali
,
et al.
Article dans une revue
hal-01610040v1
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Dlk1-Dio3 cluster miRNAs regulate mitochondrial functions in Duchenne muscular dystrophy
Ai Vu Hong
,
Nathalie Bourg
,
Peggy Sanatine
,
Jerome Poupiot
,
Karine Charton
,
et al.
Article dans une revue
hal-03454735v2
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Co-Administration of Simvastatin Does Not Potentiate the Benefit of Gene Therapy in the mdx Mouse Model for Duchenne Muscular Dystrophy
Nathalie Bourg
,
Ai Vu Hong
,
William Lostal
,
Abbass Jaber
,
Nicolas Guerchet
,
et al.
Article dans une revue
hal-03585553v1
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Different outcome of sarcoglycan missense mutation between human and mouse
Sara F Henriques
,
Cécile Patissier
,
Nathalie Bourg
,
Chiara Fecchio
,
Doriana Sandona
,
et al.
Article dans une revue
hal-02333031v1
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Species-specific titin splicing regulates cardiotoxicity associated with calpain 3 gene therapy for limb-girdle muscular dystrophy 2A
William Lostal
,
Carinne Roudaut
,
Marine Faivre
,
Karine Charton
,
Laurence Suel
,
et al.
Article dans une revue
hal-02408897v1
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A comparison of AAV strategies distinguishes overlapping vectors for efficient systemic delivery of the 6.2 kb Dysferlin coding sequence
Marina Pryadkina
,
William Lostal
,
Nathalie Bourg
,
Karine Charton
,
Carinne Roudaut
,
et al.
Article dans une revue
hal-02336876v1
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Dual Blockade of Misfolded Alpha-Sarcoglycan Degradation by Bortezomib and Givinostat Combination
Lucile Hoch
,
Nathalie Bourg
,
Fanny Degrugillier
,
Céline Bruge
,
Manon Benabides
,
et al.
Article dans une revue
hal-03874719v1
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γ-sarcoglycan and dystrophin mutation spectrum in an Algerian cohort
Evelyne Gicquel
,
Natacha Maizonnier
,
Steven Foltz
,
William Martin
,
Nathalie Bourg
,
et al.
Article dans une revue
hal-02333075v1
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NF‐NF ‐κ BB‐dependent expression of the antiapoptotic factor c‐FLIP is regulated by calpain 3, the protein involved in limb‐girdle muscular dystrophy type 2A
Béatrice Benayoun
,
Stephen Baghdiguian
,
Alicia Lajmanovich
,
Marc Bartoli
,
Nathalie Daniele
,
et al.
Article dans une revue
hal-03674309v1
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Titin splicing regulates cardiotoxicity associated with calpain 3 gene therapy for limb-girdle muscular dystrophy type 2A
William Lostal
,
Carinne Roudaut
,
Marine Faivre
,
Karine Charton
,
Laurence Suel
,
et al.
Article dans une revue
hal-03335723v1
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The Phenotype of Dysferlin-Deficient Mice Is Not Rescued by Adeno-Associated Virus–Mediated Transfer of Anoctamin 5
Florence Le Roy
,
Laurence Suel
,
Jérôme Poupiot
,
Marc Bartoli
,
François Monjaret
,
et al.
Article dans une revue
hal-02336935v1
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Dual Effects of Exercise in Dysferlinopathy
Olivier Biondi
,
Marie Villemeur
,
Alice Marchand
,
Fabrice Chrétien
,
Nathalie Bourg
,
et al.
Article dans une revue
hal-02338049v1
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Assessment of Therapeutic Potential of a Dual AAV Approach for Duchenne Muscular Dystrophy
Sonia Albini
,
Laura Palmieri
,
Auriane Dubois
,
Nathalie Bourg
,
William Lostal
,
et al.
Article dans une revue
hal-04302872v1
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A mouse model for monitoring calpain activity under physiological and pathological conditions
Marc Bartoli
,
Nathalie Bourg
,
Daniel Stockholm
,
Fabrice Raynaud
,
Antony Delevacque
,
et al.
Article dans une revue
hal-01610049v1
|
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A Naturally Occurring Human Minidysferlin Protein Repairs Sarcolemmal Lesions in a Mouse Model of Dysferlinopathy
Martin Krahn
,
Nicolas Wein
,
Marc Bartoli
,
William Lostal
,
Sebastien Courrier
,
et al.
Article dans une revue
hal-01610037v1
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Lack of Correlation between Outcomes of Membrane Repair Assay and Correction of Dystrophic Changes in Experimental Therapeutic Strategy in Dysferlinopathy
William Lostal
,
Marc Bartoli
,
Carinne Roudaut
,
Nathalie Bourg
,
Martin Krahn
,
et al.
Article dans une revue
hal-01610028v1
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A new pathway encompassing calpain 3 and its newly identified substrate cardiac ankyrin repeat protein is involved in the regulation of the nuclear factor‐κB pathway in skeletal muscle
Lydie Laure
,
Nathalie Danièle
,
Laurence Suel
,
Sylvie Marchand
,
Sophie Aubert
,
et al.
Article dans une revue
hal-01610035v1
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AAV-mediated transfer of FKRP shows therapeutic efficacy in a murine model but requires control of gene expression
Evelyne Gicquel
,
Natacha Maizonnier
,
Steven Foltz
,
William Martin
,
Nathalie Bourg
,
et al.
Article dans une revue
hal-02177575v1
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