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Publications

	Gene Therapy in Patients with the Crigler–Najjar Syndrome Lorenzo D’antiga , Ulrich Beuers , Giuseppe Ronzitti , Nicola Brunetti-Pierri , Ulrich Baumann New England Journal of Medicine, 2023, 389 (7), pp.620-631. ⟨10.1056/NEJMoa2214084⟩ Article dans une revue hal-04324294v1
	Preclinical Development of an AAV8-hUGT1A1 Vector for the Treatment of Crigler-Najjar Syndrome Fanny Collaud , Giulia Bortolussi , Laurence Guianvarc'H , Sem Aronson , Thierry Bordet Molecular Therapy - Methods and Clinical Development, 2019, 12, pp.157-174. ⟨10.1016/j.omtm.2018.12.011⟩ Article dans une revue hal-02179298v1