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Giuseppe Ronzitti

7

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1042365

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giuseppe-ronzitti
0000-0002-9184-0210
IdRef : 26470309X

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Publications

isabelle-richard

	Muscle‐specific, liver‐detargeted adeno‐associated virus gene therapy rescues Pompe phenotype in adult and neonate Gaa^−/− mice P. Sellier , P. Vidal , B. Bertin , E. Gicquel , E Bertil‐froidevaux Journal of Inherited Metabolic Disease, 2023, ⟨10.1002/jimd.12625⟩ Article dans une revue hal-04302850v1
	Dual muscle-liver transduction imposes immune tolerance for muscle transgene engraftment despite preexisting immunity Laurent Bartolo , Stéphanie Li Chung Tong , Pascal Chappert , Dominique Urbain , Fanny Collaud JCI Insight, 2019, 4 (11), ⟨10.1172/jci.insight.127008⟩ Article dans une revue hal-04324422v1
	Dual muscle-liver transduction imposes immune tolerance for muscle transgene engraftment despite preexisting immunity Laurent Bartolo , Stéphanie Li Chung Tong , Pascal Chappert , Dominique Urbain , Fanny Collaud JCI Insight, 2019, 4 (11), pii: 127008. ⟨10.1172/jci.insight.127008⟩ Article dans une revue hal-02332827v1
	Role of Regulatory T Cell and Effector T Cell Exhaustion in Liver-Mediated Transgene Tolerance in Muscle Jérôme Poupiot , Helena Costa Verdera , Romain Hardet , Pasqualina Colella , Fanny Collaud Molecular Therapy - Methods and Clinical Development, 2019, 15, pp.83-100. ⟨10.1016/j.omtm.2019.08.012⟩ Article dans une revue hal-04324398v1
	Role of Regulatory T Cell and Effector T Cell Exhaustion in Liver-Mediated Transgene Tolerance in Muscle Jérôme Poupiot , Helena Costa Verdera , Romain Hardet , Pasqualina Colella , Fanny Collaud Molecular Therapy - Methods and Clinical Development, 2019, 15, pp.83 - 100. ⟨10.1016/j.omtm.2019.08.012⟩ Article dans une revue hal-02392771v1
	Rescue of GSDIII Phenotype with Gene Transfer Requires Liver- and Muscle-Targeted GDE Expression Patrice Vidal , Serena Pagliarani , Pasqualina Colella , Helena Costa Verdera , Louisa Jauze Molecular Therapy, 2018, 26 (3), pp.890-901. ⟨10.1016/j.ymthe.2017.12.019⟩ Article dans une revue hal-04324453v1
	Rescue of GSDIII Phenotype with Gene Transfer Requires Liver- and Muscle-Targeted GDE Expression Patrice Vidal , Serena Pagliarani , Pasqualina Colella , Helena Costa Verdera , Louisa Jauze Molecular Therapy, 2018, 26 (3), pp.890-901. ⟨10.1016/j.ymthe.2017.12.019⟩ Article dans une revue hal-02332988v1