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Bioengineered AAV vectors with increased skeletal muscle potency and specificity for systemic gene therapy of myotubular myopathy
Edith Renaud-Gabardos
,
Elandari Jihad
,
Louise Mangin
,
Weinmann Jonas
,
Esther Attebi
,
et al.
ESGCT, 2021, PARIS, France
Poster de conférence
hal-04488882v1
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AAV-Mediated Gene Transfer Restores a Normal Muscle Transcriptome in a Canine Model of X-Linked Myotubular Myopathy
Jean-Baptiste Dupont
,
Jianjun Guo
,
Edith Renaud-Gabardos
,
Karine Poulard
,
Virginie Latournerie
,
et al.
Article dans une revue
hal-04291348v1
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Internal ribosome entry site-based vectors for combined gene therapy
Edith Renaud-Gabardos
,
Fransky Hantelys
,
Florent Morfoisse
,
Xavier Chaufour
,
Barbara Garmy-Susini
,
et al.
Article dans une revue
hal-03121893v1
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Apelin modulates pathological remodeling of lymphatic endothelium after myocardial infarction
Florence Tatin
,
Edith Renaud-Gabardos
,
Anne-Claire Godet
,
Fransky Hantelys
,
Françoise Pujol
,
et al.
Article dans une revue
hal-02393140v1
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Promoter-Dependent Translation Controlled by p54nrb and hnRNPM during Myoblast Differentiation
Nadera Ainaoui
,
Fransky Hantelys
,
Edith Renaud-Gabardos
,
Morgane Bunel
,
Frédéric Lopez
,
et al.
Article dans une revue
hal-03121844v1
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Periprostatic Adipose Tissue Favors Prostate Cancer Cell Invasion in an Obesity-Dependent Manner: Role of Oxidative Stress
Victor Laurent
,
Aurélie Toulet
,
Camille Attané
,
Delphine Milhas
,
Stéphanie Dauvillier
,
et al.
Article dans une revue
hal-03121906v1
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Therapeutic Benefits and Adverse Effects of Combined Pro-Angiogenic Gene Therapy in Mouse Critical Leg Ischemia.
Benoît Lebas
,
Julien Galley
,
Edith Renaud-Gabardos
,
Françoise Pujol
,
Françoise Lenfant
,
et al.
Article dans une revue
inserm-01424778v1
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Therapeutic Benefit and Gene Network Regulation by Combined Gene Transfer of Apelin, FGF2, and SERCA2a into Ischemic Heart
Edith Renaud-Gabardos
,
Florence Tatin
,
Fransky Hantelys
,
Benoît Lebas
,
Denis Calise
,
et al.
Article dans une revue
hal-02924122v1
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Biodistribution of AAVpo1 and AAVpo1A1 in mice with myotubular myopathy
Edith Renaud-Gabardos
,
Paloma Navas-Navarro
,
Jihad Elandari
,
Louise Mangin
,
Karine Poulard
,
et al.
ASGCT 2020, May 2020, Boston (MA), United States
Poster de conférence
hal-04442079v1
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Vasohibin1, a new mouse cardiomyocyte IRES trans-acting factor that regulates translation in early hypoxia
Fransky Hantelys
,
Anne-Claire Godet
,
Florian David
,
Florence Tatin
,
Edith Renaud-Gabardos
,
et al.
Article dans une revue
hal-03104359v1
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Peptide-displaying chimeric AAV vectors with increased skeletal muscle potency and liver detargeting for systemic gene therapy
Edith Renaud-Gabardos
,
Jihad El Andari
,
Louise Mangin
,
Jonas Weinmann
,
Esther Attebi
,
et al.
Myology 2022, Sep 2022, Nice, France
Poster de conférence
hal-04442190v1
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Bioengineered AAV vectors with increased skeletal muscle potency and specificity for systemic gene therapy
Edith Renaud-Gabardos
,
Jihad El Andari
,
Louise Mangin Jonas Weinmann
,
Esther Attebi
,
Emanuele Bourges
,
et al.
ASGCT 2022, May 2022, Washington DC, United States
Poster de conférence
hal-04442173v1
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Semirational bioengineering of AAV vectors with increased potency and specificity for systemic gene therapy of muscle disorders
Jihad El Andari
,
Edith Renaud-Gabardos
,
Warut Tulalamba
,
Jonas Weinmann
,
Louise Mangin
,
et al.
Science Advances , 2022, 8 (38)
Article dans une revue
hal-04273243v1
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Use of a synthetic AAV capsid for gene therapy of muscle and central nervous system disorders
Ana Buj-Bello
,
Edith Renaud-Gabardos
France, Patent n° : EP20305412.7. 2020
Brevet
hal-04482827v1
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AAV-Mediated Gene Transfer Restores a Normal Muscle Transcriptome in a Canine Model of X-Linked Myotubular Myopathy
J. B. Dupont
,
J. Guo
,
E. Renaud-Gabardos
,
K. Poulard
,
V. Latournerie
,
et al.
Article dans une revue
hal-02880796v1
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Administration of a recombinant AAVpo1A1 vector expressing MTM1 corrects skeletal muscle pathology with detargeted liver transduction in myotubular myopathy mice
Edith Renaud-Gabardos
,
Célia Sourd
,
Louise Mangin
,
Paloma Navas-Navarro
,
Jonas Weinmann
,
et al.
ESGCT, Oct 2021, Online, France
Poster de conférence
hal-04484212v1
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Adaptation de la synthèse protéique du VEGF-C par les cellules tumorales en condition hypoxique
Florent Morfoisse
,
Edith Renaud-Gabardos
,
Fransky Hantelys
,
Anne-Catherine Prats
,
Barbara Garmy-Susini
Article dans une revue
hal-03121829v1
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Local production of tenascin-C acts as a trigger for monocyte/macrophage recruitment that provokes cardiac dysfunction
Dounia Abbadi
,
Fanny Laroumanie
,
Mathilde Bizou
,
Joffrey Pozzo
,
Danièle Daviaud
,
et al.
Article dans une revue
hal-02411881v1
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Role of hypoxia and vascular endothelial growth factors in lymphangiogenesis
Florent Morfoisse
,
Edith Renaud-Gabardos
,
Fransky Hantelys
,
Anne-Catherine Prats
,
Barbara Garmy-Susini
Article dans une revue
hal-03121812v1
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