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Co-Administration of Simvastatin Does Not Potentiate the Benefit of Gene Therapy in the mdx Mouse Model for Duchenne Muscular Dystrophy

Nathalie Bourg , Ai Vu Hong , William Lostal , Abbass Jaber , Nicolas Guerchet , et al.
International Journal of Molecular Sciences, 2022, 23 (4), ⟨10.3390/ijms23042016⟩
Article dans une revue hal-03585553v1
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Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy

Caroline C. Le Guiner , Laurent Servais , Marie Montus , Thibaut Thibaut , Bodvael Fraysse , et al.
Nature Communications, 2017, 8 (1), pp.16105. ⟨10.1038/ncomms16105⟩
Article dans une revue hal-02179396v1

Epigenetic alterations in the dystrophic muscle environment down-regulate rAAV-mediated transgene expression

Jean Baptiste Dupont , Benoit Tournaire , Christophe Georger , Laetitia van Wittenberghe , Béatrice Marolleau , et al.
16. Annual Meeting of the American Society of Gene and Cell Therapy (ASGCT), May 2013, Salt Lake City, Utah, United States
Communication dans un congrès hal-02747561v1
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Short-lived recombinant adeno-associated virus transgene expression in dystrophic muscle is associated with oxidative damage to transgene mRNA

Jean-Baptiste Dupont , Benoit Tournaire , Christophe Georger , Béatrice Marolleau , Laurence Jeanson-Leh , et al.
Molecular Therapy - Methods and Clinical Development, 2015, 27 (3), pp.122-34. ⟨10.1038/mtm.2015.10⟩
Article dans une revue inserm-01799048v1

A phase I trial of adeno-associated virus serotype 1-γ-sarcoglycan gene therapy for limb girdle muscular dystrophy type 2C

France Herson , Faycal Hentati , Aude Rigolet , Anthony Behin , Norma Beatriz Romero , et al.
Brain - A Journal of Neurology , 2012, 135 (2), pp.483-492. ⟨10.1093/brain/awr342⟩
Article dans une revue hal-02179399v1

Identification of decorin derived peptides with a zinc dependent anti-myostatin activity

Simon Guiraud , Laetitia van Wittenberghe , Christophe Georger , Daniel Scherman , Antoine Kichler
Neuromuscular Disorders, 2012, 22 (12), pp.1057-1068. ⟨10.1016/j.nmd.2012.07.002⟩
Article dans une revue istex hal-02179402v1