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Evaluation of diversity indices to estimate clonal dominance in gene therapy studies

Guillaume Corre , Anne Galy
Molecular Therapy - Methods and Clinical Development, 2023, 29, pp.418-425. ⟨10.1016/j.omtm.2023.05.003⟩
Article dans une revue hal-04324363v1

464. RCL-Pooling Assay: A Simplified Method for the Detection of Replication Competent Lentiviruses in Vector Batches Using Sequential Pooling

Guillaume Corre , Corre Guillaume , Michel Dessainte , Jean-Brice Marteau , Bruno Dalle , et al.
ASGCT, 2019, washington, DC, United States. pp.S184, ⟨10.1016/S1525-0016(16)33273-7⟩
Communication dans un congrès hal-02178331v1

Quantitative proteomic analysis of lentiviral vectors using 2‐DE

Jérôme Denard , Stéphanie Rundwasser , Nicolas Laroudie , Florence Gonnet , Luigi Naldini , et al.
Proteomics, 2009, 9 (14), pp.3666-3676. ⟨10.1002/pmic.200800747⟩
Article dans une revue hal-04381121v1
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Temporary Reduction of Membrane CD4 with the Antioxidant MnTBAP Is Sufficient to Prevent Immune Responses Induced by Gene Transfer

S. da Rocha , J. Bigot , F. Onodi , Jérémie Cosette , Guillaume Corre , et al.
Mol Ther Methods Clin Dev, 2019, 14, pp.285-299. ⟨10.1016/j.omtm.2019.06.011⟩
Article dans une revue hal-02880792v1

Gene therapy on the move

K. B. Kaufmann , H. Buning , A. Galy , A. Schambach , M. Grez
EMBO Mol Med, 2013, ⟨10.1002/emmm.201202287⟩
Article dans une revue hal-02881127v1

Human syncytins can pseudotype lentiviral vectors, enabling gene transfer into B cells

M. Ferrand , Y. Coquin , A. Seye , S. Frin , E. Renaud , et al.
Human Gene Therapy, 2021, 32 (19-20), pp.A88-A89
Article dans une revue hal-03789526v1

Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome

A. Aiuti , L. Biasco , S. Scaramuzza , F. Ferrua , M. P. Cicalese , et al.
Science, 2013, 341 (6148), pp.1233151. ⟨10.1126/science.1233151⟩
Article dans une revue hal-02881198v1

MyD88 signaling in B cells regulates the production of Th1-dependent antibodies to AAV

M. Sudres , S. Cire , V. Vasseur , L. Brault , S. da Rocha , et al.
Molecular Therapy, 2012, 20 (8), pp.1571-81. ⟨10.1038/mt.2012.101⟩
Article dans une revue hal-02881210v1

The Wiskott-Aldrich syndrome protein permits assembly of a focused immunological synapse enabling sustained T-cell receptor signaling

R. Calvez , F. Lafouresse , J. de Meester , A. Galy , S. Valitutti , et al.
Haematologica, 2011, 96 (10), pp.1415-1423. ⟨10.3324/haematol.2011.040204⟩
Article dans une revue hal-03765488v1
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Biosafety Studies of a Clinically Applicable Lentiviral Vector for the Gene Therapy of Artemis-SCID

S. Charrier , C. Lagresle-Peyrou , V. Poletti , M. Rothe , G. Cedrone , et al.
Mol Ther Methods Clin Dev, 2019, 15, pp.232-245. ⟨10.1016/j.omtm.2019.08.014⟩
Article dans une revue hal-02880790v1

Gene therapy for Wiskott-Aldrich syndrome in a severely affected adult

E. C. Morris , T. Fox , R. Chakraverty , R. Tendeiro , K. Snell , et al.
Blood, 2017, 130 (11), pp.1327-1335. ⟨10.1182/blood-2017-04-777136⟩
Article dans une revue hal-02881008v1

Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome

Alessandro Aiuti , Luca Biasco , Samantha Scaramuzza , Francesca Ferrua , Maria Pia Cicalese , et al.
Science, 2013, 341 (6148), ⟨10.1126/science.1233151⟩
Article dans une revue hal-03765427v1

Wiskott-Aldrich syndrome protein-deficient hematopoietic cells can be efficiently mobilized by granulocyte colony-stimulating factor

S. Charrier , M. Blundell , G. Cedrone , F. Louache , W. Vainchenker , et al.
Haematologica, 2013, 98 (8), pp.1300-8. ⟨10.3324/haematol.2012.077040⟩
Article dans une revue hal-02881150v1

Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia

Paula Río , Susana Navarro , Wei Wang , Rebeca Sánchez-Domínguez , Roser M. Pujol , et al.
Nature Medicine, 2019, 25, pp.1396-1401. ⟨10.1038/s41591-019-0550-z⟩
Article dans une revue hal-02880813v1
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Recent advances using genetic therapies against infectious diseases and for vaccination

Anne Galy , Ben Berkhout , Karine Breckpot , Chantal Pichon , Kristie Bloom , et al.
Human Gene Therapy, 2023, ⟨10.1089/hum.2023.123⟩
Article dans une revue hal-04197730v1
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Increased production of pro-inflammatory cytokines and enhanced T cell responses after activation of human dendritic cells with IL-1 and CD40 ligand.

Amy Wesa , Anne Galy
BMC Immunology, 2002, 3, pp.14
Article dans une revue inserm-00123511v1

Efficacité et sécurité du traitement par thérapie génique des patients atteints du syndrome de Wiskott-Aldrich

Anne Galy , Guillaume Corre , Marina Cavazzana , Salima Hacein-Bey-Abina
Médecine/Sciences, 2015, 31 (12), pp.1066-1069. ⟨10.1051/medsci/20153112006⟩
Article dans une revue hal-02178298v1

Gene therapy for the Wiskott-Aldrich syndrome

A. Galy , A. J. Thrasher
Curr Opin Allergy Clin Immunol, 2011, 11 (6), pp.545-50. ⟨10.1097/ACI.0b013e32834c230c⟩
Article dans une revue hal-02881154v1

Twelfth Annual Meeting of the French Society of Cell and Gene Therapy

Els Verhoeyen , Sophie Gomez , Anne Galy , Eduard Ayuso , Patrick Midoux , et al.
Human Gene Therapy, 2016, 27 (7), pp.555-558. ⟨10.1089/hum.2016.29031.eve⟩
Article dans une revue hal-01469045v1

Like Angler Fish, CAARs Lure Their Prey

A. Galy
Molecular Therapy, 2016, 24 (8), pp.1339-41. ⟨10.1038/mt.2016.165⟩
Article dans une revue hal-02880980v1

Major Advances in the Development of Vectors for Clinical Gene Therapy of Hematopoietic Stem Cells from European Groups over the Last 25 Years

A. Galy
Human Gene Therapy, 2017, 28 (11), pp.964-971. ⟨10.1089/hum.2017.152⟩
Article dans une revue hal-02880981v1

Vectofusin-1 Improves Transduction of Primary Human Cells with Diverse Retroviral and Lentiviral Pseudotypes, Enabling Robust, Automated Closed-System Manufacturing

C. Radek , O. Bernadin , K. Drechsel , N. Cordes , R. Pfeifer , et al.
Human Gene Therapy, 2019, 30, pp.1477-1493. ⟨10.1089/hum.2019.157⟩
Article dans une revue hal-02880812v1

Toward a Scalable Purification Protocol of GaLV-TR-Pseudotyped Lentiviral Vectors

D. Boudeffa , B. Bertin , A. Biek , M. Mormin , F. Leseigneur , et al.
Hum Gene Ther Methods, 2019, 30, pp.153-171. ⟨10.1089/hgtb.2019.076⟩
Article dans une revue hal-02880786v1

Vectofusin-1 Promotes RD114-TR-Pseudotyped Lentiviral Vector Transduction of Human HSPCs and T Lymphocytes

C. Piovan , V. Marin , C. Scavullo , S. Corna , E. Giuliani , et al.
Mol Ther Methods Clin Dev, 2017, 5, pp.22-30. ⟨10.1016/j.omtm.2017.02.003⟩
Article dans une revue hal-02881009v1

Outcomes following gene therapy in patients with severe Wiskott-Aldrich syndrome

Salima Hacein-Bey Abina , H Bobby Gaspar , Johanna Blondeau , Laure Caccavelli , Sabine Charrier , et al.
Journal of the American Medical Association, 2015, 313 (15), pp.1550-63. ⟨10.1001/jama.2015.3253⟩
Article dans une revue hal-02880982v1

Non-Clinical Efficacy and Safety Studies on G1XCGD, a Lentiviral Vector for Ex Vivo Gene Therapy of X-Linked Chronic Granulomatous Disease

Christian Brendel , Michael Rothe , Giorgia Santilli , Sabine Charrier , Stefan Stein , et al.
Human gene therapy. Clinical development, 2018, 29 (2), pp.69-79. ⟨10.1089/humc.2017.245⟩
Article dans une revue hal-03765483v1

Stem cell gene therapy for fanconi anemia: report from the 1st international Fanconi anemia gene therapy working group meeting

J. Tolar , J. E. Adair , M. Antoniou , C. C. Bartholomae , P. S. Becker , et al.
Molecular Therapy, 2011, 19 (7), pp.1193-8. ⟨10.1038/mt.2011.78⟩
Article dans une revue hal-02881136v1

Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients

S Charrier , L Dupré , S Scaramuzza , L Jeanson-Leh , M Blundell , et al.
Gene Therapy, 2007, 14 (5), pp.415-428. ⟨10.1038/sj.gt.3302863⟩
Article dans une revue hal-03765501v1

Quantification of lentiviral vector copy numbers in individual hematopoietic colony-forming cells shows vector dose-dependent effects on the frequency and level of transduction

S. Charrier , M. Ferrand , M. Zerbato , G. Precigout , A. Viornery , et al.
Gene Ther, 2011, 18 (5), pp.479-87. ⟨10.1038/gt.2010.163⟩
Article dans une revue hal-02881185v1
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Immune Response and Intraocular Inflammation in Patients With Leber Hereditary Optic Neuropathy Treated With Intravitreal Injection of Recombinant Adeno-Associated Virus 2 Carrying the ND4 Gene

Céline Bouquet , Catherine Vignal Clermont , Anne Galy , Serge Fitoussi , Laure Blouin , et al.
JAMA Ophthalmology, 2019, 137 (4), pp.399. ⟨10.1001/jamaophthalmol.2018.6902⟩
Article dans une revue hal-02131584v1